医学
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10 篇有效样本 · 按发表日期由新到旧排列
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Selective targeting of RSK signaling with PMD-026 suppresses FLT3-activated acute myeloid leukemia while sparing normal hematopoiesis
作者Gavin M. Traber; Kailen Mark; Aarthi Jayanthan; Hee-Don Chae; Minyoung Youn; Jenny Youm; Nick J. Sharp; Sandra E. Dunn; Kathleen M. Sakamoto
作者单位1. Division of Hematology/Oncology, Department of Pediatrics, Stanford University School of Medicine, Stanford, USA; 2. Phoenix Molecular Designs, San Diego, USA
Spatial remodeling of bone marrow architecture defines tissue-state signatures of disease activity and therapeutic response in myelodysplastic neoplasms
作者Ryan Nachman; Aleksandra Kopacz; Caitlin Unkenholz; Jian Chai; Arvin Ruiz; Itzel Valencia; Jeanne Jiang; Fabio Socciarelli; Jiwoon Park; Christopher E. Mason; Ling Zhang; David Sallman; Gail J. Roboz; Pinkal Desai; Justin Kaner; Joshua Fein; Monica Guzman; Neal Lindeman; Amy Chadburn; Madhu Ouseph; Paul Simonson; Julia Geyer; Giorgio Inghirami; Shahin Rafii; David Redmond; Sanjay S. Patel
作者单位1. Division of Regenerative Medicine, Department of Medicine, Hartman Institute for Therapeutic Organ Regeneration, Ansary Stem Cell Institute, Weill Cornell Medicine, New York, USA; 2. Multiparametric In Situ Imaging (MISI) Laboratory, Department of Pathology and Laboratory Medicine, Weill Cornell Medicine, New York, USA; 3. Division of Hematopathology, Department of Pathology and Laboratory Medicine, Weill Cornell Medicine/NewYork-Presbyterian Hospital, New York, USA; 4. Immunopathology Laboratory, Weill Cornell Medical College/NewYork-Presbyterian Hospital, New York, USA; 5. Department of Physiology and Biophysics, Weill Cornell Medicine, New York, USA; 6. The Feil Family Brain and Mind Research Institute, Weill Cornell Medicine, New York, USA; 7. WorldQuant Initiative for Quantitative Prediction, Weill Cornell Medicine, New York, USA; 8. The HRH Prince Alwaleed Bin Talal Bin Abdulaziz Alsaud Institute for Computational Biomedicine, Weill Cornell Medicine, New York, USA; 9. Department of Hematopathology and Laboratory Medicine, Moffitt Cancer Center, Tampa, USA; 10. Department of Malignant Hematology, Moffitt Cancer Center, Tampa, USA; 11. Division of Hematology and Medical Oncology, Department of Medicine, Weill Cornell Medicine/NewYork-Presbyterian Hospital, New York, USA; 12. Division of Molecular Genetic Pathology, Department of Pathology and Laboratory Medicine, Weill Cornell Medicine/NewYork-Presbyterian Hospital, New York, USA
Lineage-restricted dependency on an oncofetal SNHG29 -IGF2BP1 RNA axis in acute megakaryoblastic leukemia
作者Robert Winkler; Bruno Griesler; Wolfgang Sippl; Reinier A. Boon; Stefanie Dimmeler; Ilka Wittig; Marie-Laure Yaspo; Stefan Hüttelmaier; Raj Bhayadia; Dirk Heckl; Jan-Henning Klusmann
作者单位1. Department of Pediatrics, Goethe University Frankfurt, Frankfurt am Main, Germany; 2. Frankfurt Cancer Institute, Frankfurt/Main, Germany; 3. German Cancer Consortium (DKTK), German Cancer Research Center (DKFZ), Partner site, Frankfurt/Mainz, Germany; 4. Institute of Molecular Medicine, Martin Luther University Halle-Wittenberg, Halle, Germany; 5. University Clinic and Outpatient Clinic for Internal Medicine IV, University Medicine Halle (Saale), Halle (Saale), Germany; 6. Institute for Cardiovascular Regeneration, Centre for Molecular Medicine, Goethe University, Frankfurt Am Main, Germany; 7. German Centre for Cardiovascular Research, Partner Site Frankfurt Rhein/Main, Frankfurt, Germany; 8. Department of Physiology, Amsterdam University Medical Centers, Vrije Universiteit Amsterdam, Amsterdam, the Netherlands; 9. Amsterdam Cardiovascular Sciences, Amsterdam, the Netherlands; 10. Max Planck Institute for Molecular Genetics, Berlin, Germany; 11. School of Health Sciences and Technology, UPES, Dehradun, India; 12. Institute for Experimental Pediatric Hematology and Oncology, Goethe University Frankfurt, Frankfurt am Main, Germany
FATP2-mediated lipid metabolism enhances chimeric antigen receptor T-cell therapy resistance in B-cell acute lymphoblastic leukemia
作者Clarissa Garcia; Kaylyn U. Lyons; Julian Grandvallet Contreras; Tian Liu; Alexis J. Donnelly; Amanda J. Novak; Amy Argabright; Colin Anderson; Abby Grier; Sabrina Smith; Joshua Michlin; Jesutomisin Olusoji; Railey G. Mikeska; Xin Zhou; Huimin Geng; Jeremy T. Rahkola; Hiten N. Patel; Jeffrey G. Jacot; Markus Müschen; Angelo D’Alessandro; John E. Dick; Ilaria Iacobucci; Charles G. Mullighan; Julie A. Reisz; Tzu Phang; M. Eric Kohler; Matthew T. Witkowski
作者单位1. Department of Pediatrics, University of Colorado Anschutz Medical Campus, Aurora, USA; 2. Department of Biochemistry and Molecular Genetics, University of Colorado Anschutz Medical Campus, Aurora, USA; 3. Department of Molecular Genetics, University of Toronto, Princess Margaret Hospital, University Health Network, Princess Margaret Cancer Research Tower, Toronto, Canada; 4. Department of Pathology, St Jude Children’s Research Hospital, Memphis, USA; 5. Department of Laboratory Medicine, University of California San Francisco, San Francisco, USA; 6. Rocky Mountain Regional Veteran Affairs Medical Center, Aurora, USA; 7. Department of Bioengineering, University of Colorado Anschutz Medical Campus, Aurora, USA; 8. Division of Pediatrics, Children’s Hospital Colorado, Aurora, USA; 9. Center of Molecular and Cellular Oncology, Yale Cancer Center, Yale University, New Haven, USA; 10. Division of Blood and Marrow Transplant & Cellular Therapeutics, Center for Cancer and Blood Disorders, Children’s Hospital Colorado, Aurora, USA; 11. Division of Hematology, University of Colorado Anschutz Medical Campus, Aurora, USA
Selective sensitivity of Ph-like B-cell acute lymphoblastic leukemia to BRG1 inhibition identifies a therapeutic vulnerability
作者V. S. S. Abhinav Ayyadevara; Ria Perencsik; Shreya Patil; Shikha Gaur; Ashley Paik; Monika Toma; Gerald Wertheim; Huimin Geng; Tomasz Skorski; Srividya Swaminathan; Christian Hurtz
作者单位1. Department of Basic Science, Division of Cancer Sciences, Loma Linda University School of Medicine, Loma Linda, USA; 2. University of British Columbia, Vancouver, Canada; 3. Southern Adventist University, Collegedale, USA; 4. Fels Cancer Institute for Personalized Medicine, Lewis Katz School of Medicine, Temple University Philadelphia, Philadelphia, USA; 5. Department of Pathology and Laboratory Medicine, University of Pennsylvania Perelman School of Medicine, Philadelphia, USA; 6. Department of Laboratory Medicine, University of California, San Francisco, USA; 7. Department of Cancer and Cellular Biology, Lewis Katz School of Medicine, Temple University Philadelphia, Philadelphia, USA; 8. Nuclear Dynamics and Cancer Program, Fox Chase Cancer Center, Philadelphia, USA; 9. Department of Systems Biology, City of Hope Beckman Research Institute, Duarte, USA; 10. Department of Pediatrics, City of Hope Beckman Research Institute, Duarte, USA
From data to evidence: why administrative databases alone cannot measure real-world effectiveness in rare diseases – the case of chronic myeloid leukaemia
作者Sara Mucherino; Enrica Menditto; Valentina Orlando
作者单位1. Department of Pharmacy, University of Naples Federico II, Naples, Italy; 2. CIRFF, Centre of Pharmacoeconomics and Drug Utilization Research, University of Naples Federico II, Naples, Italy
CircZBTB46, a promising therapeutic target in crizotinib resistant ALK-positive T lymphomas
作者Loélia Babin; Elissa Andraos; Steffen Fuchs; Chloe Bessière; Lola Colras; Sandra Dailhau; Cathy Quelen; Cindy Pinto; Iyad Daoudi; Romain Pfeifer; Ahmed Zamani; Marina Bousquet; Stéphane Pyronnet; Christine Gaspin; Laurence Lamant; Fabienne Meggetto
作者单位1. Univ Toulouse, CNRS, INSERM, CRCT (Cancer Research Center of Toulouse), UMR-1037, UMR-5071, Institut Universitaire du Cancer, Toulouse, France; 2. Laboratoire d’Excellence Toulouse Cancer-TOUCAN, Toulouse, France; 3. Department of Pediatric Oncology and Hematology, Charité - Universitätsmedizin, Corporate Member of Freie Universität Berlin and Humboldt-Universität, Berlin, Germany; 4. German Cancer Consortium (DKTK), Partner Site Berlin, a Partnership Between DKFZ and Charité-Universitätsmedizin, Berlin Institute of Health at Charité – Universitätsmedizin Berlin, Berlin, Germany; 5. INRAE, BioinfOmics, GenoToul Bioinformatics Facility, Université de Toulouse, Castanet-Tolosan, Toulouse, France; 6. INRAE, MIAT, Université de Toulouse, Castanet-Tolosan, Toulouse, France
MYD88 variants in chronic lymphocytic leukemia exhibit distinct biological behaviors and prognostic implications
作者Yuting Yan; Yulan Zhou; Weihao Chen; Jun Wang; Tingyu Wang; Ying Yu; Wenjie Xiong; Yujiao Jia; Zhen Yu; Dehui Zou; Gang An; Lugui Qiu; Fei Li; Shuhua Yi
作者单位1. State Key Laboratory of Experimental Hematology, National Clinical Research Center for Blood Diseases, Haihe Laboratory of Cell Ecosystem, Institute of Hematology& Blood Diseases Hospital, Chinese Academy of Medical Sciences & Peking Union Medical College, Tianjin, China; 2. Tianjin Institutes of Health Science, Tianjin, China; 3. Jiangxi Provincial Key Laboratory of Hematological Diseases, Department of Hematology, The First Affiliated Hospital, Jiangxi Medical College, Nanchang University, Nanchang, China; 4. Institute of Hematology, Academy of Clinical Medicine of Jiangxi Province, Nanchang, China
Small interfering RNA-mediated silencing of mutant NPM1 suppresses acute myeloid leukemia via reversing KAT7 and p300-mediated histone acetylation
作者Yongqiang Hou; Yunzhi Xing; Chunjie Chen; Dongxue Su; Zhien Zhou; Yi Ye; Zhangjian Lai; Zhixian Peng; Hongxi Cai; Min Sun; Yue Liu; Bingying Yang; Haitao Huang; Zhe Li; Jinhuan Li; Junhong Li; Huan Gao; Jiaxin Li; Hao Zhao; Yiran Shi; Qinghua Chen; Jun Long; Jiong Hu; Dawang Zhou; Lanfen Chen
作者单位1. State Key Laboratory of Cellular Stress Biology, School of Life Sciences, Xiang’an Hospital, Xiang An Biomedicine Laboratory, Faculty of Medicine and Life Sciences, Xiamen University, Xiamen, China; 2. Department of Hematology, Tongji Hospital, School of Medicine, Tongji University, Shanghai, China; 3. Shanghai Institute of Hematology Blood & Marrow Transplantation Center, Department of Hematology, Collaborative Innovation Center of Hematology, Rui Jin Hospital Affiliated to Shanghai Jiao Tong University School of Medicine, Shanghai, China
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