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35最短天数
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全部论文审稿周期

4 篇有效样本 · 按发表日期由新到旧排列
审稿天数=录用日期-收稿日期;保留 PDF/DOI/网页源链接

114 天

Antisense Oligonucleotide STK-002 Increases OPA1 in Retina and Improves Mitochondrial Function in Autosomal Dominant Optic Atrophy Cells

作者
Aditya Venkatesh; Taylor McKenty; Syed Ali; Donna Sonntag; Shobha Ravipaty; Yanyan Cui; Deirdre Slate; Qian Lin; Anne Christiansen; Sarah Jacobson; Jacob Kach; Kian Huat Lim; Vaishnavi Srinivasan; Boris Zinshteyn; Isabel Aznarez; Laryssa A. Huryn; Zhiyu Li; Robert B. Hufnagel; Gene Liau; Karen Anderson; Jeff Hoger展开收起
作者单位
1. Stoke Therapeutics, Bedford, Massachusetts, USA.; 2. Ophthalmic Genetics and Visual Function Branch, National Eye Institute, National Institutes of Health, Bethesda, Maryland, USA.展开收起
官方全文证据 DOI 网页
141 天

Next Generation Exon 51 Skipping Antisense Oligonucleotides for Duchenne Muscular Dystrophy

作者
Judith van Deutekom; Chantal Beekman; Suzanne Bijl; Sieto Bosgra; Rani van den Eijnde; Dennis Franken; Bas Groenendaal; Bouchra Harquouli; Anneke Janson; Paul Koevoets; Melissa Mulder; Daan Muilwijk; Galyna Peterburgska; Bianca Querido; Janwillem Testerink; Ruurd Verheul; Peter de Visser; Rudie Weij; Annemieke Aartsma-Rus; Jukka Puoliväli; Timo Bragge; Charles O'Neill; Nicole A. Datson展开收起
作者单位
1. VICO Therapeutics B.V., formerly BioMarin Nederland B.V., Leiden, The Netherlands.; 2. Department of Human Genetics, Leiden University Medical Centre, Leiden, The Netherlands.; 3. Charles River Discovery Services, Kuopio, Finland.; 4. BioMarin Pharmaceutical, Inc., San Rafael, California, USA.展开收起
官方全文证据 DOI 网页
117 天

Time Is a Critical Factor When Evaluating Oligonucleotide Therapeutics in hERG Assays

作者
Yusheng Qu; Robert Kirby; Richard Davies; Ayesha Jinat; Stefano Stabilini; Bin Wu; Longchuan Yu; BaoXi Gao; Hugo M. Vargas展开收起
作者单位
1. Amgen Research, Translational Safety and Bioanalytical Sciences, Amgen, Inc., Thousand Oaks, California, USA.; 2. Metrion Biosciences Ltd, Granta Center, Cambridge, United Kingdom.; 3. Hybrid Modality Engineering, Amgen, Inc., Thousand Oaks, California, USA.; 4. Cardiometabolic Disorders, Amgen, Inc., Thousand Oaks, California, USA.展开收起
官方全文证据 DOI 网页
35 天

Consensus Guidelines for the Design and In Vitro Preclinical Efficacy Testing N-of-1 Exon Skipping Antisense Oligonucleotides

作者
Annemieke Aartsma-Rus; Alejandro Garanto; Willeke van Roon-Mom; Erin M. McConnell; Victoria Suslovitch; Winston X. Yan; Jonathan K. Watts; Timothy W. Yu展开收起
作者单位
1. Dutch Center for RNA Therapeutics, the Netherlands.; 2. Department of Human Genetics, Leiden University Medical Center, Leiden, the Netherlands.; 3. N = 1 Collaborative.; 4. Department of Pediatrics and Department of Human Genetics, Radboud Institute for Molecular Life Sciences, Radboud University Medical Center, Nijmegen, the Netherlands.; 5. Department of Genetics and Genomics, Boston Children's Hospital, Boston, Massachusetts, USA.; 6. RNA Therapeutics Institute, UMass Chan Medical School, Worcester, Massachusetts, USA.; 7. Harvard Medical School, Division of Genetics and Genomics, Boston, Massachusetts, USA.展开收起
官方全文证据 DOI 网页

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平均审稿62 天

中位数65 天

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