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Review Cycle Records

MOLECULAR THERAPY

Elsevier SCIE 非OA
2026新锐 1区2025中科院 1区 TOP2025 JCR Q1
198.4平均天数
190.5中位天数
137最短天数
287最长天数
5582025发文量

Paper Review Records

全部论文审稿周期

10 篇有效样本 · 按发表日期由新到旧排列
审稿天数=录用日期-收稿日期;保留 PDF/DOI/网页源链接

279 天

miR-146a mimic therapy protects against platelet-mediated thrombosis

作者Sonia Águila; Juan C. García-Cañaveras; Laura Zapata-Martínez; Ana B. Arroyo; Nuria García-Barberá; Salvador Carrillo-Tornel; Pedro J. Guijarro-Carrillo; Paula González-Jiménez; Ana Latorre; María L. Lozano; Bernard Payrastre; José Rivera; Marie-Pierre Gratacap; Raúl Méndez; Agustín Lahoz; Marcin Kortylewski; Rocío González-Conejero; Constantino Martínez

作者单位Centro Regional de Hemodonación, Servicio de Hematología Hospital Universitario Morales Meseguer, IMIB Pascual Parrilla, 30003 Murcia, Spain; Universidad de Murcia, 30100 Murcia, Spain; ImuBi, Universidad de Murcia, 30100 Murcia, Spain; Biomarkers and Precision Medicine Unit, Instituto de Investigación Sanitaria Fundación Hospital La Fe, 46026 Valencia, Spain; Pneumology Department, La Fe University and Polytechnic Hospital, 46026 Valencia, Spain; Respiratory Infections, Health Research Institute La Fe (IISLAFE), 46026 Valencia, Spain; Medicine Department, University of Valencia. 46026 Valencia, Spain; INSERM, UMR-S U1297 and University of Toulouse III, Institute of Cardiovascular and Metabolic Diseases (I2MC), CHU-Rangueil, 31432 Toulouse, France; Laboratoire d'Hématologie, CHU de Toulouse, 31059 Toulouse Cedex, France; Centro de Investigación Biomédica en Red de Enfermedades Respiratorias (CIBERES), Instituto de Salud Carlos III, 28029 Madrid, Spain; Center for Gene Therapy and Department of Immuno-Oncology, Beckman Research Institute at City of Hope Comprehensive Cancer Center, Duarte, CA 91010, USA

PDF源文件 DOI 网页
148 天

Functional editing of the OTC locus by targeted integration with phenotype correction and restoration of endogenous expression patterns

作者Samantha L. Ginn; Fatemeh Doroudian; Sharntie Christina; Otilia P.Y. Chan; Caitlin W. Lucas; Erhua Zhu; Sile F. Yang; Beena Devanapalli; Anne H. Klein; Suzanne Scott; Joseph Vitale; Sharon C. Cunningham; Sophia H.Y. Liao; Marti Cabanes-Creus; Leszek Lisowski; Ian E. Alexander

作者单位Gene Therapy Research Unit, Children’s Medical Research Institute, Faculty of Medicine and Health, The University of Sydney and Sydney Children’s Hospitals Network, Westmead, NSW 2145, Australia; NSW Biochemical Genetics Service, The Children’s Hospital at Westmead, Westmead, NSW 2145, Australia; Australian e-Health Research Centre, Commonwealth Scientific and Industrial Research Organisation (CSIRO), Herston, QLD 4006, Australia; Translational Vectorology Research Unit, Children’s Medical Research Institute, Faculty of Medicine and Health, The University of Sydney and Sydney Children’s Hospitals Network, Westmead, NSW 2145, Australia; Laboratory of Molecular Oncology and Innovative Therapies, Military Institute of Medicine, National Research Institute, 04-141 Warszawa, Poland; Discipline of Child and Adolescent Health, Sydney Medical School, Faculty of Medicine and Health, The University of Sydney, Westmead, NSW 2145, Australia

PDF源文件 DOI 网页
197 天

Programmable engineered bacteria manipulate metabolism and remodel the TME in situ for enhancing adoptive cell therapy

作者Jin Chen; Tianliang Liu; Xiumin Liu; Hongyue Zhang; Chen Wang; Yuan Meng; Miaoqing Wu; Sachiyo Nomura; Zhe Zhang; Songcheng Yin; Changhua Zhang; Aoran Dong

作者单位Department of Medical Oncology, Fudan University Shanghai Cancer Center, Shanghai 200032, China; College of Pharmaceutical Sciences, Soochow Medical College of Soochow University, Soochow University, Suzhou 215123, China; Shanghai Key Laboratory of Cancer Systems Regulation and Clinical Translation, Jiading District Central Hospital, Renji Hospital Jiading Branch, Shanghai 201822, China; Digestive Diseases Center, The Seventh Affiliated Hospital Sun Yat-sen University, Shenzhen, Guangdong 518107, China; LifeX Institute, School of Medical Technology, Gannan Medical University, Ganzhou, Jiangxi 341000, China; Henan University of Science and Technology, Luoyang, Henan 471023, China; Department of Gastrointestinal Surgery, Graduate School of Medicine, The University of Tokyo, Tokyo, Japan

PDF源文件 DOI 网页
160 天

Distinct YY dinucleotide periodicity in adeno-associated virus DNA

作者Conradin Baumgartl; Jonas Becker; Lena Naber; Man Xu; Emma Gerstmann; Julie Garcia Gonzalez-Calero; Joyce Suppacher; Sebastian Heß; Felix Bubeck; Dirk Grimm

作者单位Department of Infectious Diseases/Virology, Section Viral Vector Technologies, Medical Faculty, Heidelberg University, BioQuant, Center for Integrative Infectious Diseases (CIID), 69120 Heidelberg, Germany; AbbVie Deutschland GmbH & Co. KG, 67061 Ludwigshafen, Germany; German Center for Infection Research (DZIF) and German Center for Cardiovascular Research (DZHK), Partner Site Heidelberg, 69120 Heidelberg, Germany; Faculty of Engineering Sciences, Heidelberg University, 69120 Heidelberg, Germany

PDF源文件 DOI 网页
147 天

Long-term functional synaptic integration of genome-edited retinal organoids in a primate model of macular degeneration

作者Atsuta Ozaki; Akihiro Kawai; Ryutaro Akiba; Satoko Okayama; Nobuhiko Ohno; Keisuke Kajita; Tomohiro Masuda; Satoshi Yokota; Shin-ichiro Ito; Du Peiyan; Kenta Onoue; Shigenobu Yonemura; Mineo Kondo; Yasuo Kurimoto; Yingbin Fu; Michiko Mandai

作者单位Kobe City Eye Hospital, Kobe 650-0047, Japan; Cell and Gene Therapy in Ophthalmology Laboratory, BZP, RIKEN, Wako, Saitama 351-0198, Japan; Department of Ophthalmology, Mie University Graduate School of Medicine, Tsu 514-8507, Japan; Ophthalmology and Visual Science, Chiba University Graduate School of Medicine, Chiba 260-8670, Japan; Laboratory for Ultrastructural Research, RIKEN Center for Biosystems Dynamics Research, Kobe 650-0047, Japan; Division of Ultrastructural Research, National Institute for Physiological Sciences, Okazaki 444-8787, Japan; Department of Anatomy, Division of Histology and Cell Biology, Jichi Medical University, Shimotsuke 329-0498, Japan; Department of Ophthalmology, Institute of Biomedical Sciences, Tokushima University Graduate School, Tokushima 770-8503, Japan; Laboratory for Animal Resources and Genetic Engineering, RIKEN Center for Biosystems Dynamics Research, Kobe 650-0047, Japan; Department of Cell Biology, Tokushima University Graduate School of Medicine, Tokushima 770-8503, Japan; Cullen Eye Institute, Baylor College of Medicine, Houston, TX 77030, USA

PDF源文件 DOI 网页
195 天

A compact GAD67 promoter enables inhibitory neuron-targeted AAV gene therapy for seizure suppression

作者Yuuki Fukai; Ayumu Konno; Nobutake Hosoi; Karin Miyakawa; Ryosuke Kaneko; Hirokazu Hirai

作者单位Viral Vector Core, Gunma University, Initiative for Advanced Research, Maebashi, Gunma 371-8511, Japan; Department of Neurophysiology & Neural Repair, Gunma University Graduate School of Medicine, Maebashi, Gunma 371-8511, Japan; Medical Genetics Research Center, Nara Medical University, 840 Shijo-Cho, Kashihara, Nara 634-8521, Japan

PDF源文件 DOI 网页
248 天

Increasing intrinsic protein disorder improves CD8+ immunogenicity for a SARS CoV2 vaccine candidate antigen

作者Li Wan; Bingxian Xie; Masahiro Shuda; Maura E. O'Malley; Carlos J. Camacho; Greg M. Delgoffe; Yuan Chang; Patrick S. Moore

作者单位Cancer Virology Program, Hillman Cancer Center, University of Pittsburgh, Pittsburgh, PA 15232, USA; Immunology Program, Hillman Cancer Center, University of Pittsburgh, Pittsburgh, PA 15232, USA; Department of Computational and Systems Biology, University of Pittsburgh, Pittsburgh, PA 15232, USA

PDF源文件 DOI 网页
137 天

Cerebrospinal delivery of a bidirectional AAV9 vector improves optic nerve and retinal pathology in a sheep model of Tay-Sachs disease

作者Brett D. Story; Sara M. Thomasy; Sara A. Adelman; Toloo Taghian; Yvette Lopez; Monica Ardon; Hikaru Shiraishi; Sabina Khan; Meher Khan; Maria Do; Hector R. Benatti; Stephanie Bertrand; Rachel Prestigiacomo; Rachael Gately; Douglas R. Martin; Miguel Sena-Esteves; Jun Xie; Guangping Gao; Leandro B.C. Teixeira; Gillian C. Shaw; Nicholas Marsh-Armstrong; Heather L. Gray-Edwards

作者单位Department of Surgical and Radiological Sciences, School of Veterinary Medicine, University of California–Davis, Davis, CA 95616, USA; Department of Ophthalmology & Vision Science, University of California, Davis, Sacramento, CA 95817, USA; Department of Genetic and Cellular Medicine, University of Massachusetts Medical School, Worcester, MA 01605, USA; Tufts Farm, Cummings School of Veterinary Medicine, Tufts University, North Grafton, MA 01536, USA; Department of Pathobiological Sciences, School of Veterinary Medicine, University of Wisconsin-Madison, Madison, WI 53706, USA; Department of Ambulatory and Theriogenology, Cummings School of Veterinary Medicine, Tufts University, North Grafton, MA 01536, USA; Scott-Ritchey Research Center, Auburn University College of Veterinary Medicine, Auburn, AL 36849, USA; Department of Radiology, University of Massachusetts Medical School, Worcester, MA 01605, USA

PDF源文件 DOI 网页
186 天

Antibody format matters: A comparative analysis of VHH and scFv domains reveals superior in vivo CAR T cell function with VHH domains

作者Alexander Kinna; Preeta Datta; Reyisa Bughda; Farhaan Parekh; Mathew Robson; Ram Jha; Phillip Wu; Ian Scott; Elizabeth Hogben; Oliver Amin; Gordon Weng-Kit Cheung; Warren Hazelton; Zulaikha Akbar; Katarina Lamb; Emily Macken; Chris Allen; Sofi Panovska; Lisa Hogan; Mohamed El-Kholy; Reevesh Shrestha; Jonathan Popplewell; Evangelia Kokalaki; James Sillibourne; Simon Thomas; Shimobi Onuoha; Mathieu Ferrari; Martin Pule

作者单位Autolus Therapeutics Plc, London W12 7FP, UK; Developmental Biology and Cancer Department, The Cancer Institute, Paul O’Gorman Building, University College London, London WC1E 6DD, UK; Carterra Inc, Salt Lake City, UT 84103, USA

PDF源文件 DOI 网页
287 天

Depletion of CD8+ CART cells leads to superior anti-tumor efficacy of pure CD4+ CART cells against acute leukemias

作者Qian Chen; David Sedloev; Hao Yao; Lianghao Mao; Dominic Depke; Lei Wang; Marina Scheller; Bailin He; Yi Liu; Julia M. Unglaub; Anita Schmitt; Ashok Kumar Jayavelu; Carsten Müller-Tidow; Michael Schmitt; Tim Sauer

作者单位Department of Medicine V, Hematology, Oncology and Rheumatology, University Hospital Heidelberg, 69120 Heidelberg, Germany; Department of Lymphoma, Zhejiang Cancer Hospital, Hangzhou Institute of Medicine (HIM), Chinese Academy of Sciences, Hangzhou 310022, China; Proteomics and Cancer Cell Signaling Group, Clinical Cooperation Unit Pediatric Leukemia, German Cancer Research Center and Department of Pediatric Oncology, Hematology and Immunology, University of Heidelberg, 69120 Heidelberg, Germany; Department of Hematology, Nanfang Hospital, Southern Medical University, Guangzhou 510515, China; Hopp Children’s Cancer Center, 69120 Heidelberg, Germany

PDF源文件 DOI 网页

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《融合机器学习与生命周期评价的城市污水处理碳排放预测与优化》

样本口径2026 年最近 5 篇有效论文样本

平均审稿96.4 天

中位数77 天

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